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Journal article
Event-free survival of maralixibat-treated patients with Alagille syndrome compared to a real-world cohort from GALA
Hansen, Bettina E.
Vandriel, Shannon M.
Vig, Pamela
Garner, Will
Mogul, Douglas B.
Loomes, Kathleen M.
Piccoli, David A.
Rand, Elizabeth B.
Jankowska, Irena
Czubkowski, Piotr
Gliwicz-Miedzińska, Dorota
Gonzales, Emmanuel M.
Jacquemin, Emmanuel
Bouligand, Jérôme
D’Antiga, Lorenzo
Nicastro, Emanuele
Arnell, Henrik
Fischler, Björn
Sokal, Etienne
[UCL]
Demaret, Tanguy
[UCL]
Siew, Susan
Stormon, Michael
Karpen, Saul J.
Romero, Rene
Ebel, Noelle H.
Feinstein, Jeffrey A.
Roberts, Amin J.
Evans, Helen M.
Sundaram, Shikha S.
Chaidez, Alexander
Hardikar, Winita
Shankar, Sahana
Fischer, Ryan T.
Lacaille, Florence
Debray, Dominique
Lin, Henry C.
Jensen, M. Kyle
Jaramillo, Catalina
Karthikeyan, Palaniswamy
Indolfi, Giuseppe
Verkade, Henkjan J.
Larson-Nath, Catherine
Quiros-Tejeira, Ruben E.
Valentino, Pamela L.
Rogalidou, Maria
Dezsőfi, Antal
Squires, James E.
Schwarz, Kathleen
Calvo, Pier Luigi
Bernabeu, Jesus Quintero
Zizzo, Andréanne N.
Nebbia, Gabriella
Bulut, Pinar
Santos-Silva, Ermelinda
Fawaz, Rima
Nastasio, Silvia
Karnsakul, Wikrom
Tamara, María Legarda
Busoms, Cristina Molera
Kelly, Deirdre A.
Sandahl, Thomas Damgaard
Jimenez-Rivera, Carolina
Banales, Jesus M.
Mujawar, Quais
Li, Li-Ting
She, Huiyu
Wang, Jian-She
Kim, Kyung Mo
Oh, Seak Hee
Sanchez, Maria Camila
Cavalieri, Maria Lorena
Lee, Way Seah
Hajinicolaou, Christina
Lertudomphonwanit, Chatmanee
Waisbourd-Zinman, Orith
Arikan, Cigdem
Alam, Seema
Carvalho, Elisa
Melere, Melina
Eshun, John
Önal, Zerrin
Desai, Dev M.
Wiecek, Sabina
Pinto, Raquel Borges
Wolters, Victorien M.
Garcia, Jennifer
Beretta, Marisa
Kerkar, Nanda
Brecelj, Jernej
Rock, Nathalie
Lurz, Eberhard
Blondet, Niviann
Shah, Uzma
Thompson, Richard J.
Kamath, Binita M.
(2024)
Hepatology — Vol. 79, no. 6, p. 1279-1292 (2024)