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Displaying 23 results.
    • Journal article
    Natural History of Liver Disease in a Large International Cohort of Children with Alagille syndrome: Results from The <scp>GALA</scp> Study
    Vandriel, Shannon M. Li, Li‐Ting She, Huiyu Wang, Jian‐She Gilbert, Melissa A. Jankowska, Irena Czubkowski, Piotr Gliwicz‐Miedzińska, Dorota Gonzales, Emmanuel M. Jacquemin, Emmanuel Bouligand, Jérôme Spinner, Nancy B. Loomes, Kathleen M. Piccoli, David A. D'Antiga, Lorenzo Nicastro, Emanuele Sokal, Etienne[UCL] Demaret,Tanguy Ebel, Noelle H. Feinstein, Jeffrey A. Fawaz, Rima Nastasio, Silvia Lacaille, Florence Debray, Dominique Arnell, Henrik Fischler, Björn Siew, Susan Stormon, Michael Karpen, Saul J. Romero, Rene Kim, Kyung Mo Baek, Woo Yim Hardikar, Winita Shankar, Sahana Roberts, Amin J. Evans, Helen M. Jensen, M. Kyle Kavan, Marianne Sundaram, Shikha S. Chaidez, Alexander Karthikeyan, Palaniswamy Sanchez, Maria Camila Cavalieri, Maria Lorena Verkade, Henkjan J. Lee, Way Seah Squires, James E. Hajinicolaou, Christina Lertudomphonwanit, Chatmanee Fischer, Ryan T. Larson‐Nath, Catherine Mozer‐Glassberg, Yael Arikan, Cigdem Lin, Henry C. Quintero Bernabeu, Jesus Alam, Seema Kelly, Deirdre Carvalho, Elisa Ferreira, Cristina Targa Indolfi, Giuseppe Quiros‐Tejeira, Ruben E. Bulut, Pinar Calvo, Pier Luigi Önal, Zerrin Valentino, Pamela L. Desai, Dev M. Eshun, John Rogalidou, Maria Dezsőfi, Antal Wiecek, Sabina Nebbia, Gabriella Borges Pinto, Raquel Wolters, Victorien M. Tamara, María Legarda Zizzo, Andréanne N. Garcia, Jennifer Schwarz, Kathleen Beretta, Marisa Sandahl, Thomas Damgaard Jimenez‐Rivera, Carolina Kerkar, Nanda Brecelj, Jernej Mujawar, Quais Rock, Nathalie Busoms, Cristina Molera Karnsakul, Wikrom Lurz, Eberhard Santos‐Silva, Ermelinda Blondet, Niviann Bujanda, Luis Shah, Uzma Thompson, Richard J. Hansen, Bettina E. Kamath, Binita M. (2023) Hepatology — Vol. 77, no. 2, p. 512-529 (2023)
    • Journal article
    Event-free survival of maralixibat-treated patients with Alagille syndrome compared to a real-world cohort from GALA
    Hansen, Bettina E. Vandriel, Shannon M. Vig, Pamela Garner, Will Mogul, Douglas B. Loomes, Kathleen M. Piccoli, David A. Rand, Elizabeth B. Jankowska, Irena Czubkowski, Piotr Gliwicz-Miedzińska, Dorota Gonzales, Emmanuel M. Jacquemin, Emmanuel Bouligand, Jérôme D’Antiga, Lorenzo Nicastro, Emanuele Arnell, Henrik Fischler, Björn Sokal, Etienne[UCL] Demaret, Tanguy Siew, Susan Stormon, Michael Karpen, Saul J. Romero, Rene Ebel, Noelle H. Feinstein, Jeffrey A. Roberts, Amin J. Evans, Helen M. Sundaram, Shikha S. Chaidez, Alexander Hardikar, Winita Shankar, Sahana Fischer, Ryan T. Lacaille, Florence Debray, Dominique Lin, Henry C. Jensen, M. Kyle Jaramillo, Catalina Karthikeyan, Palaniswamy Indolfi, Giuseppe Verkade, Henkjan J. Larson-Nath, Catherine Quiros-Tejeira, Ruben E. Valentino, Pamela L. Rogalidou, Maria Dezsőfi, Antal Squires, James E. Schwarz, Kathleen Calvo, Pier Luigi Bernabeu, Jesus Quintero Zizzo, Andréanne N. Nebbia, Gabriella Bulut, Pinar Santos-Silva, Ermelinda Fawaz, Rima Nastasio, Silvia Karnsakul, Wikrom Tamara, María Legarda Busoms, Cristina Molera Kelly, Deirdre A. Sandahl, Thomas Damgaard Jimenez-Rivera, Carolina Banales, Jesus M. Mujawar, Quais Li, Li-Ting She, Huiyu Wang, Jian-She Kim, Kyung Mo Oh, Seak Hee Sanchez, Maria Camila Cavalieri, Maria Lorena Lee, Way Seah Hajinicolaou, Christina Lertudomphonwanit, Chatmanee Waisbourd-Zinman, Orith Arikan, Cigdem Alam, Seema Carvalho, Elisa Melere, Melina Eshun, John Önal, Zerrin Desai, Dev M. Wiecek, Sabina Pinto, Raquel Borges Wolters, Victorien M. Garcia, Jennifer Beretta, Marisa Kerkar, Nanda Brecelj, Jernej Rock, Nathalie Lurz, Eberhard Blondet, Niviann Shah, Uzma Thompson, Richard J. Kamath, Binita M. (2023) Hepatology — (2023)