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Journal article
Two-Year Outcomes of Valoctocogene Roxaparvovec Therapy for Hemophilia A.
Mahlangu, Johnny
Kaczmarek, Radoslaw
von Drygalski, Annette
Shapiro, Susan
Chou, Sheng-Chieh
Ozelo, Margareth C
Kenet, Gili
Peyvandi, Flora
Wang, Michael
Madan, Bella
Key, Nigel S
Laffan, Michael
Dunn, Amy L
Mason, Jane
Quon, Doris V
Symington, Emily
Leavitt, Andrew D
Oldenburg, Johannes
Chambost, Hervé
Reding, Mark T
Jayaram, Kala
Yu, Hua
Mahajan, Reena
Chavele, Konstantia-Maria
Reddy, Divya B
Henshaw, Joshua
Robinson, Tara M
Wong, Wing Yen
Pipe, Steven W
GENEr8-1 Trial Group
Hermans, Cédric
[UCL]
(2023)
The New England journal of medicine — Vol. 388, no.8, p. 694-705 (2023)