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    • Journal article
    Event-free survival of maralixibat-treated patients with Alagille syndrome compared to a real-world cohort from GALA
    Hansen, Bettina E. Vandriel, Shannon M. Vig, Pamela Garner, Will Mogul, Douglas B. Loomes, Kathleen M. Piccoli, David A. Rand, Elizabeth B. Jankowska, Irena Czubkowski, Piotr Gliwicz-Miedzińska, Dorota Gonzales, Emmanuel M. Jacquemin, Emmanuel Bouligand, Jérôme D’Antiga, Lorenzo Nicastro, Emanuele Arnell, Henrik Fischler, Björn Sokal, Etienne[UCL] Demaret, Tanguy Siew, Susan Stormon, Michael Karpen, Saul J. Romero, Rene Ebel, Noelle H. Feinstein, Jeffrey A. Roberts, Amin J. Evans, Helen M. Sundaram, Shikha S. Chaidez, Alexander Hardikar, Winita Shankar, Sahana Fischer, Ryan T. Lacaille, Florence Debray, Dominique Lin, Henry C. Jensen, M. Kyle Jaramillo, Catalina Karthikeyan, Palaniswamy Indolfi, Giuseppe Verkade, Henkjan J. Larson-Nath, Catherine Quiros-Tejeira, Ruben E. Valentino, Pamela L. Rogalidou, Maria Dezsőfi, Antal Squires, James E. Schwarz, Kathleen Calvo, Pier Luigi Bernabeu, Jesus Quintero Zizzo, Andréanne N. Nebbia, Gabriella Bulut, Pinar Santos-Silva, Ermelinda Fawaz, Rima Nastasio, Silvia Karnsakul, Wikrom Tamara, María Legarda Busoms, Cristina Molera Kelly, Deirdre A. Sandahl, Thomas Damgaard Jimenez-Rivera, Carolina Banales, Jesus M. Mujawar, Quais Li, Li-Ting She, Huiyu Wang, Jian-She Kim, Kyung Mo Oh, Seak Hee Sanchez, Maria Camila Cavalieri, Maria Lorena Lee, Way Seah Hajinicolaou, Christina Lertudomphonwanit, Chatmanee Waisbourd-Zinman, Orith Arikan, Cigdem Alam, Seema Carvalho, Elisa Melere, Melina Eshun, John Önal, Zerrin Desai, Dev M. Wiecek, Sabina Pinto, Raquel Borges Wolters, Victorien M. Garcia, Jennifer Beretta, Marisa Kerkar, Nanda Brecelj, Jernej Rock, Nathalie Lurz, Eberhard Blondet, Niviann Shah, Uzma Thompson, Richard J. Kamath, Binita M. (2023) Hepatology — (2023)